Gene therapy companies
Companies whose enriched business profile is tagged “Gene therapy”, drawn from their SEC filings + website text. Sorted by market capitalization; every figure is delayed data from SEC EDGAR + Finnhub, shown with its as-of date.
- NOVARTIS AG (NVS) — Global pharmaceutical and biotechnology company pioneering disease-modifying treatments across oncology, immunology, neuroscience, and rare genetic diseases. ask →
- PTC THERAPEUTICS INC (PTCT) Health Care — PTC Therapeutics develops precision medicines and gene therapies targeting rare genetic disorders and serious diseases, generating revenue from approved products and partnered collaboration deals. ask →
- CRISPR THERAPEUTICS AG (CRSP) Health Care — CRISPR Therapeutics develops gene-editing medicines using CRISPR/Cas9 technology, with the first approved CRISPR therapy (CASGEVY) for sickle cell disease and beta thalassemia, plus a pipeline of in vivo and cell therapy programs. ask →
- VOR BIOPHARMA INC (VOR) Health Care — Vor Biopharma is a clinical-stage biopharmaceutical company developing advanced cell therapy and gene therapy solutions for blood disorders and cancers. ask →
- XOMA ROYALTY CORP (XOMA) Health Care — A lean-infrastructure royalty aggregator that generates non-dilutive capital for biotech developers in exchange for long-duration milestone and royalty rights across a diversified 120+ asset portfolio spanning oncology, rare disease, and specialty therapeutics. ask →
- BENITEC BIOPHARMA INC (BNTC) Health Care — Benitec is a clinical-stage gene therapy company developing DNA-directed RNA interference (ddRNAi) treatments delivered via adeno-associated viral vectors to potentially provide "one-shot" cures for genetic diseases. ask →
- ROCKET PHARMACEUTICALS INC (RCKT) Health Care — Rocket Pharmaceuticals develops AAV and lentiviral gene therapies for rare genetic and cardiac diseases with a focus on monogenic disorders. ask →
- Fractyl Health, Inc. (GUTS) Health Care — Fractyl Health is a clinical-stage medical device and gene therapy company developing the Revita mucosa resurfacing procedure and Rejuva gene therapy platform for type 2 diabetes and metabolic disorders. ask →
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Data: SEC EDGAR (filings) + Finnhub (fundamentals, delayed daily-close). Figures shown with their as-of date.
Last updated 2026-07-21.
Informational only — NOT financial advice. All figures are delayed daily-close data from SEC EDGAR & Finnhub, shown with their as-of date.