genetic medicine companies

Companies whose enriched business profile is tagged “genetic medicine”, drawn from their SEC filings + website text. Sorted by market capitalization; every figure is delayed data from SEC EDGAR + market data, shown with its as-of date.

• BioMarin Pharmaceutical (BMRN) Health Care — BioMarin is a biotechnology leader dedicated to transforming the lives of patients with rare, genetically defined diseases through innovative, category-defining medicines. ask →
• BEAM THERAPEUTICS INC (BEAM) Health Care — Beam Therapeutics is a biotechnology firm pioneering base editing technology to create next-generation precision genetic medicines. ask →
• Sarepta Therapeutics (SRPT) Health Care — Sarepta Therapeutics is a leader in genetic medicine, specializing in innovative RNA-targeted and gene therapies to treat rare neuromuscular diseases like Duchenne muscular dystrophy. ask →
• WAVE LIFE SCIENCES LTD (WVE) Health Care — Wave Life Sciences is a clinical-stage biotech company developing stereopure nucleic acid therapeutics via its proprietary PRISM platform to treat genetically defined diseases. ask →
• FULCRUM THERAPEUTICS INC (FULC) Health Care — Fulcrum Therapeutics is a clinical-stage biopharmaceutical company focused on unlocking gene expression to treat serious, rare genetic diseases. ask →
• CAMP4 THERAPEUTICS CORP (CAMP) Health Care — CAMP4 Therapeutics is a clinical-stage biopharmaceutical company developing RNA-targeting therapies to upregulate gene expression and restore protein levels for patients with genetic diseases. ask →
• SIONNA THERAPEUTICS INC (SION) Health Care — Sionna Therapeutics is a clinical-stage biopharma company pioneering NBD1-stabilizing therapies to treat the underlying cause of cystic fibrosis. ask →
• ENTRADA THERAPEUTICS INC (TRDA) Health Care — Entrada Therapeutics is developing a new class of intracellular genetic medicines using its proprietary endosomal escape vehicle technology to treat serious neuromuscular and retinal diseases. ask →
• PepGen Inc. (PEPG) Health Care — PepGen is a clinical-stage biotechnology company developing peptide-enhanced oligonucleotide therapies to treat severe neuromuscular diseases, with a primary focus on Myotonic Dystrophy Type 1. ask →

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Data: SEC EDGAR (filings) + market data (fundamentals, delayed daily-close). Figures shown with their as-of date.

Last updated 2026-10-08.

Informational only — NOT financial advice. All figures are delayed daily-close data from SEC EDGAR & market data, shown with their as-of date.